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Longitudinal quantitative muscle magnetic resonance imaging (qMRI) in five boys with Duchenne muscular dystrophy (DMD), on and off treatment With drisapersen
Longitudinal quantitative muscle MRI in 5 Duchenne boys on and off drisapersen treatment
Longitudinal quantitative muscle MRI in 5 Duchenne boys on and off drisapersen treatment
DMD transcript imbalance determines dystrophin levels
Dystrophin levels do not influence disease progression in Becker muscular dystrophy patients with an exon 45-47 deletion
Inter- and intra muscle fat fraction variability in DMD patients