Persistent URL of this record https://hdl.handle.net/1887/97114
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Effect of enzyme therapy and prognostic factors in 69 adults with Pompe disease: an open-label single-center study
- All authors
- Vries, J.M. de; Beek, N.A.M.E. van der; Hop, W.C.J.; Karstens, F.P.J.; Wokke, J.H.; Visser, M. de; Engelen, B.G.M. van; Kuks, J.B.M.; Kooi, A.J. van der; Notermans, N.C.; Faber, C.G.; Verschuuren, J.J.G.M.; Kruijshaar, M.E.; Reuser, A.J.J.; Doorn, P.A. van; Ploeg, A.T. van der
- Date
- 2012-09-26
- Volume
- 7
- Pages
- -