Persistent URL of this record https://hdl.handle.net/1887/114495
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Facilitating orphan drug development: Proceedings of the TREAT-NMD International Conference, December 2015, Washington, DC, USA
- All authors
- Hoffman, E.P.; Bonnemann, C.; Boutin, M.; Brais, B.; Buccella, F.; Burghes, A.; Coffey, C.; Dasgupta, N.; Dawkins, H.; Luca, A. de; Dowd, C.; Duong, T.; Eagle, M.; Finkel, R.; Furlong, P.; Gagnon, C.; Goemans, N.; Guglieri, M.; Hathout, Y.; Johnson, N.; Kakkis, E.; Kaufmann, P.; Kimmelman, J.; Korngut, L.; Kullman, J.; Lochmuller, H.; Marini, S.; McDonald, C.; Mohan, C.; Morgenroth, L.; Morizono, H.; Nagaraju, K.; Porter, J.; Reilly, L.; Ruegg, M.; Schneider, J.; Spitali, P.; Straub, V.; Sweeney, L.; Tasca, G.; Turner, C.; Veldhuizen, O.; Verschuuren, J.; Ward, S.; Willmann, R.; TREAT-NMD Alliance
- Date
- 2017-07-31
- Journal
- Neuromuscular Disorders
- Volume
- 27
- Issue
- 7
- Pages
- 693 - 701