Preclinical Safety and Efficacy of Human CD34(+) Cells Transduced With Lentiviral Vector for the Treatment of Wiskott-Aldrich Syndrome

Author(s):
Scaramuzza, S.; Biasco, L.; Ripamonti, A.; Castiello, M.C.; Loperfido, M.; Draghici, E.; Hernandez, R.J.; Benedicenti, F.; Radrizzani, M.; Salomoni, M.; Ranzani, M.; Bartholomae, C.C.; Vicenzi, E.; Finocchi, A.; Bredius, R.; Bosticardo, M.; Schmidt, M.; Kalle, C. von; Montini, E.; Biffi, A.; Roncarolo, M.G.; Naldini, L.; Villa, A.; Aiuti, A.
Published
2013
Publication type
Article / Letter to editor
Date issued
2013-01-31
Language
English
Is part of
Molecular Therapy (2013), Vol. 21, no. 1, p. 175-184
hdl
1887/98365
doi
10.1038/mt.2012.23