Hepatic-targeted RNA interference provides robust and persistent knockdown of alpha-1 antitrypsin levels in ZZ patients

Author(s):
Turner, A.M.; Stolk, J.; Bals, R.; Lickliter, J.D.; Hamilton, J.; Christianson, D.R.; Given, B.D.; Burdon, J.G.; Loomba, R.; Stoller, J.K.; Teckman, J.H.
Published
2018
Publication type
Article / Letter to editor
siRNAPhase 1PiZZRNAiTherapeutic
Date issued
2018-08-31
Language
English
Is part of
Journal of Hepatology (2018), Vol. 69, no. 2, p. 378-384
hdl
1887/96058
doi
10.1016/j.jhep.2018.03.012