Delivery is key: lessons learnt from developing splice-switching antisense therapies

Author(s):
Godfrey, C.; Desviat, L.R.; Smedsrod, B.; Pietri-Rouxel, F.; Denti, M.A.; Disterer, P.; Lorain, S.; Nogales-Gadea, G.; Sardone, V.; Anwar, R.; Andaloussi, S. el; Lehto, T.; Khoo, B.; Brolin, C.; Roon-Mom, W.M.C. van; Goyenvalle, A.; Aartsma-Rus, A.; Arechavala-Gomeza, V.
Published
2017
Publication type
Article / Letter to editor
antisense oligonucleotidesdeliverypre-clinical modelsRNA therapytoxicity
Date issued
2017-05-31
Language
English
Is part of
EMBO Molecular Medicine (2017), Vol. 9, no. 5, p. 545-557
hdl
1887/94901
doi
10.15252/emmm.201607199