Long-term follow-up of IPEX syndrome patients after different therapeutic strategies: An international multicenter retrospective study

Author(s):
Barzaghi, F.; Hernandez, L.C.A.; Neven, B.; Ricci, S.; Kucuk, Z.Y.; Bleesing, J.J.; Nademi, Z.; Slatter, M.A.; Ulloa, E.R.; Shcherbina, A.; Roppelt, A.; Worth, A.; Silva, J.; Aiuti, A.; Murguia-Favela, L.; Speckmann, C.; Carneiro-Sampaio, M.; Fernandes, J.F.; Baris, S.; Ozen, A.; Karakoc-Aydiner, E.; Kiykim, A.; Schulz, A.; Steinmann, S.; Notarangelo, L.D.; Gambineri, E.; Lionetti, P.; Shearer, W.T.; Forbes, L.R.; Martinez, C.; Moshous, D.; Blanche, S.; Fisher, A.; Ruemmele, F.M.; Tissandier, C.; Ouachee-Chardin, M.; Rieux-Laucat, F.; Cavazzana, M.; Qasim, W.; Lucarelli, B.; Albert, M.H.; Kobayashi, I.; Alonso, L.; Heredia, C.D. de; Kanegane, H.; Lawitschka, A.; Seo, J.J.; Gonzalez-Vicent, M.; Diaz, M.A.; Goyal, R.K.; Sauer, M.G.; Yesilipek, A.; Kim, M.; Yilmaz-Demirdag, Y.; Bhatia, M.; Khlevner, J.; Padilla, E.J.R.; Martino, S.; Montin, D.; Neth, O.; Molinos-Quintana, A.; Valverde-Fernandez, J.; Broides, A.; Pinsk, V.; Ballauf, A.; Haerynck, F.; Bordon, V.; Dhooge, C.; Garcia-Lloret, M.L.; Bredius, R.G.; Kawak, K.; Haddad, E.; Seidel, M.G.; Duckers, G.; Pai, S.Y.; Dvorak, C.C.; Ehl, S.; Locatelli, F.; Goldman, F.; Gennery, A.R.; Cowan, M.J.; Roncarolo, M.G.; Bacchetta, R.; PIDTC; IEWP; European Soc Blood Marrow
Published
2018
Publication type
Article / Letter to editor
IPEXprimary immune deficiencyFOXP3Treg cellshematopoietic stem cell transplantationimmunosuppressionrapamycinenteropathyneonatal diabetesgenetic autoimmunity
Date issued
2018-03-31
Language
English
Is part of
Journal of Allergy and Clinical Immunology (2018), Vol. 141, no. 3, p. 1036-+
hdl
1887/78620
doi
10.1016/j.jaci.2017.10.041
URL
https://reader.elsevier.com/reader/sd/pii/S0091674917318936?token=F98F76335D6609A532B7707096C586F89473AA5C6A4B7A2CDCCDB1E0B8315F1D2B519E1E0116661CFCD9E2AF37EB5A27