Limitations of drug registries to evaluate orphan medicinal products for the treatment of lysosomal storage disorders

Author(s):: Hollak, C.E.M.; Aerts, J.M.F.G. (0000-0001-8168-2565); Ayme, S.; Manuel, J.

Published: 2011
Publication type: Article / Letter to editor

Date issued: 2011-04-16
Language: English
Is part of: Orphanet Journal of Rare Diseases (2011), Vol. 6, p. 16
hdl: 1887/61931
doi: 10.1186/1750-1172-6-16