'N of 1' therapies need a better model

Author(s):
Aartsma-Rus, A.
Published
2021
Publication type
Article / Letter to editor

Abstract

Oligonucleotides offer therapeutic potential for patients with genetic disorders carrying unique mutations, but developing individualized therapies is not supported by the current process for drug development.

Date issued
2021-05-24
Language
English
Publisher
NATURE RESEARCH
Is part of
Nature Medicine (2021), Vol. 27, no. 6, p. 939-939
hdl
1887/3212846
doi
10.1038/s41591-021-01380-z