Lentiviral gene therapy using cellular promoters cures type 1 Gaucher disease in mice
Author(s):
Dahl, M.; Doyle, A.; Olsson, K.; Mansson, J.E.; Marques, A.R.A.; Mirzaian, M.; Aerts, J.M.F.G. (0000-0001-8168-2565); Ehinger, M.; Rothe, M.; Modlich, U.; Schambach, A.; Karlsson, S.
