Boosting delivery of rare disease therapies: the IRDiRC Orphan Drug Development Guidebook

Author(s):
Jonker, A.H.; Hivert, V.; Gabaldo, M.; Batista, L.; O'Connor, D.; Aartsma-Rus, A.; Day, S.; Sakushima, K.; Ardigo, D.
Published
2020
Publication type
Article / Letter to editor

Abstract

The International Rare Diseases Research Consortium (IRDiRC) has created a Guidebook to facilitate drug development for rare diseases by organizing available tools into a standardized framework.

Date issued
2020-08-01
Language
English
Publisher
NATURE RESEARCH
Is part of
Nature Reviews Drug Discovery (2020), Vol. 19, no. 8, p. 495-496
hdl
1887/3184629
doi
10.1038/d41573-020-00060-w