Lyso-Gb3 is not a predictive biomarker of treatment response in migalastat-treated patients with migalastat-amenable variants

Author(s):
Schiffmann, R.; Bichet, D.G.; Aerts, J.M.F.G. (0000-0001-8168-2565); Skuban, N.; Mehta, A.B.
Published
2020
Publication type
Abstract
Date issued
2020-02-01
Language
English
Publisher
ACADEMIC PRESS INC ELSEVIER SCIENCE
Is part of
Molecular Genetics and Metabolism (2020), Vol. 129, no. 2, p. S144
hdl
1887/3142316
doi
10.1016/j.ymgme.2019.11.381