Severe Lipodystrophy Following Prolonged Subcutaneous Administration of Antisense Oligonucleotides

Author(s):
Nguyen, A.L.; Morren, M.A.; Doorn, R. van
Published
2019
Publication type
Article / Letter to editor

Abstract

This case report describes a severe adverse event following antisense oligonucleotide treatment for muscular dystrophy that occurred in 6 pediatric patients.

Date issued
2019-09-01
Language
English
Publisher
AMER MEDICAL ASSOC
Is part of
hdl
1887/123013
doi
10.1001/jamadermatol.2019.1404