Autologous Stem-Cell-Based Gene Therapy for Inherited Disorders: State of the Art and Perspectives

Author(s):
Staal, F.J.T. (0000-0003-1588-8519); Aiuti, A.; Cavazzana, M.
Published
2019
Publication type
Article / Letter to editor
gene therapySCIDthalassemiasickle cell diseasegene editinglysosomal storage disorderclinical trialcurative treatment
Date issued
2019-10-31
Language
English
Is part of
Frontiers in Pediatrics
hdl
1887/121176
doi
10.3389/fped.2019.00443