Facilitating orphan drug development: Proceedings of the TREAT-NMD International Conference, December 2015, Washington, DC, USA
- Author(s):
- Hoffman, E.P.; Bonnemann, C.; Boutin, M.; Brais, B.; Buccella, F.; Burghes, A.; Coffey, C.; Dasgupta, N.; Dawkins, H.; Luca, A. de; Dowd, C.; Duong, T.; Eagle, M.; Finkel, R.; Furlong, P.; Gagnon, C.; Goemans, N.; Guglieri, M.; Hathout, Y.; Johnson, N.; Kakkis, E.; Kaufmann, P.; Kimmelman, J.; Korngut, L.; Kullman, J.; Lochmuller, H.; Marini, S.; McDonald, C.; Mohan, C.; Morgenroth, L.; Morizono, H.; Nagaraju, K.; Porter, J.; Reilly, L.; Ruegg, M.; Schneider, J.; Spitali, P. (0000-0003-2783-688X); Straub, V.; Sweeney, L.; Tasca, G.; Turner, C.; Veldhuizen, O.; Verschuuren, J.; Ward, S.; Willmann, R.; TREAT-NMD Alliance
- Published
- 2017
- Publication type
- Article / Letter to editor
- Date issued
- 2017-07-31
- Language
- English
- Is part of
- Neuromuscular Disorders (2017), Vol. 27, no. 7, p. 693-701
- hdl
- 1887/114495
- doi
- 10.1016/j.nmd.2017.02.013