Aggregated N-of-1 trials for unlicensed medicines for small populations: an assessment of a trial with ephedrine for myasthenia gravis

Author(s):
Weinreich, S.S.; Vrinten, C.; Kuijpers, M.R.; Lipka, A.F.; Schimmel, K.J.M.; Zwet, E.W. van (0000-0001-5537-3179); Gispen-de Wied, C.; Hekster, Y.A.; Verschuuren, J.J.G.M. (0000-0002-4572-1501); Cornel, M.C.
Published
2017
Publication type
Article / Letter to editor
N-of-1 trialsHealth insurance reimbursementDrug approvalEphedrineMyasthenia gravisOff-label useDrug rediscoveryPersonalized medicineTechnology assessment (biomedical)Rare diseases
Date issued
2017-05-12
Language
English
Is part of
Orphanet Journal of Rare Diseases
hdl
1887/114491
doi
10.1186/s13023-017-0636-y