Therapeutic NOTCH3 cysteine correction in CADASIL using exon skipping: in vitro proof of concept

Author(s):: Rutten, J.W.; Dauwerse, H.G.; Peters, D.J.M. (0000-0001-6974-7143); Goldfarb, A.; Venselaar, H.; Haffner, C.; Ommen, G.J.B. van; Aartsma-Rus, A.M.; Oberstein, S.A.J.L.

Published: 2016
Publication type: Article / Letter to editor

CADASILNOTCH3exon skippingtherapycysteines

Date issued: 2016-04-30
Language: English
Is part of: Brain (2016), Vol. 139, p. 1123-1135
hdl: 1887/113748
doi: 10.1093/brain/aww011