Antisense-mediated exon skipping: Taking advantage of a trick from Mother Nature to treat rare genetic diseases

Author(s):: Veltrop, M.; Aartsma-Rus, A.

Published: 2014
Publication type: Article / Letter to editor

Rare diseaseExon skippingSplicingAntisense oligonucleotides

Date issued: 2014-07-01
Language: English
Is part of: Experimental Cell Research (2014), Vol. 325, no. 1, p. 50-55
hdl: 1887/104716
doi: 10.1016/j.yexcr.2014.01.026