The TREAT-NMD Duchenne Muscular Dystrophy Registries: Conception, Design, and Utilization by Industry and Academia

Author(s):
Bladen, C.L.; Rafferty, K.; Straub, V.; Monges, S.; Moresco, A.; Dawkins, H.; Roy, A.; Chamova, T.; Guergueltcheva, V.; Korngut, L.; Campbell, C.; Dai, Y.; Barisic, N.; Kos, T.; Brabec, P.; Rahbek, J.; Lahdetie, J.; Tuffery-Giraud, S.; Claustres, M.; Leturcq, F.; Yaou, R. ben; Walter, M.C.; Schreiber, O.; Karcagi, V.; Herczegfalvi, A.; Viswanathan, V.; Bayat, F.; Sarmiento, I.D.G.; Ambrosini, A.; Ceradini, F.; Kimura, E.; Bergen, J.C. van den; Rodrigues, M.; Roxburgh, R.; Lusakowska, A.; Oliveira, J.; Santos, R.; Neagu, E.; Butoianu, N.; Artemieva, S.; Rasic, V.M.; Posada, M.; Palau, F.; Lindvall, B.; Bloetzer, C.; Karaduman, A.; Topaloglu, H.; Inal, S.; Oflazer, P.; Stringer, A.; Shatillo, A.V.; Martin, A.S.; Peay, H.; Flanigan, K.M.; Salgado, D.; Rekowski, B. von; Lynn, S.; Heslop, E.; Gainotti, S.; Taruscio, D.; Kirschner, J.; Verschuuren, J.; Bushby, K.; Beroud, C.; Lochmuller, H.
Published
2013
Publication type
Article / Letter to editor
Duchenne muscular dystrophyDMDrare diseasedisease registriesTREAT-NMD
Date issued
2013-11-30
Language
English
Is part of
Human Mutation (2013), Vol. 34, no. 11, p. 1449-1457
hdl
1887/100815
doi
10.1002/humu.22390