Translating the Genomics Revolution: The Need for an International Gene Therapy Consortium for Monogenic Diseases
- Author(s):
- Tremblay, J.P.; Xiao, X.; Aartsma-Rus, A.; Barbas, C.; Blaus, H.M.; Bogdanove, A.J.; Boycott, K.; Brauns, S.; Breakefield, X.O.; Bueren, J.A.; Buschmann, M.; Byrne, B.J.; Calos, M.; Cathomen, T.; Chamberlain, J.; Chuah, M.; Cornetta, K.; Davies, K.E.; Dickson, J.G.; Duchateau, P.; Flotte, T.R.; Gaudet, D.; Gersbach, C.A.; Gilbert, R.; Glorioso, J.; Herzog, R.W.; High, K.A.; Huang, W.L.; Huard, J.; Joung, J.K.; Liu, D.P.; Liu, D.X.; Lochmuller, H.; Lustig, L.; Martens, J.; Massie, B.; Mavilio, F.; Mendell, J.R.; Nathwani, A.; Ponder, K.; Porteus, M.; Puymirat, J.; Samulski, J.; Takeda, S.; Thrasher, A.; VandenDriessche, T.; Wei, Y.Q.; Wilson, J.M.; Wilton, S.D.; Wolfe, J.H.; Gao, G.P.
- Published
- 2013
- Publication type
- Article / Letter to editor
- Date issued
- 2013-02-28
- Language
- English
- Is part of
- Molecular Therapy (2013), Vol. 21, no. 2, p. 266-268
- hdl
- 1887/100093
- doi
- 10.1038/mt.2013.4
